Human Gene Therapy
Central Nervous System-Targeted Gene Therapy for the Treatment of Neurocognitive Deficits in Mucopolysaccharidosis Type II Mice
Guoqing Chen
1
,
Xia Zhan
1
,
Xiaolan Gao
1
,
Mengni Yi
1
,
Huan Liang
1
,
Yixiong Chen
2
,
Qing Lin
2
,
Jun Yang
1
,
Shule Hou
1
,
Gustavo Maegawa
3
,
Huiwen Zhang
1
1
2
Lingyi Biotech Co., Ltd., Shanghai, China
3
Department of Pediatrics, Vagelos College of Physician & Surgeons, Columbia University Irving Medical Center, New York, New York, USA.
Publication type: Journal Article
Publication date: 2025-02-27
Journal:
Human Gene Therapy
scimago Q2
SJR: 1.091
CiteScore: 6.5
Impact factor: 3.9
ISSN: 10430342, 15577422
Are you a researcher?
Create a profile to get free access to personal recommendations for colleagues and new articles.